A closer look at gene therapy with PTC Therapeutics

 In the latest instalment of the pharmaphorum podcast, Editor in Chief Jonah Comstock connects with Kylie O’Keefe to talk about gene therapy in rare diseases. 

They discuss what different gene therapies have in common and how some particular therapies work. They also talk about what gene therapy means for the industry and for patients, in particularly the paradigm shift of disease-modifying therapies.