BMT for Treatment of Rare Diseases: New Treatments and Donor Options

A marrow or cord blood transplant could be the best treatment option, and for some patients, offer the only potential cure, when facing life-threatening diseases.

A FACT accredited (Foundation of the Accreditation of Cellular Therapy) program and a National Marrow Donor Program (NMDP) unrelated and cord blood donor center, Children’s Mercy Kansas City is a leader in research and the treatment of rare and complex diseases using bone marrow, peripheral blood stem cells and cord blood transplants. The program offers autologous, related allogeneic, unrelated allogeneic, and haplo-identical transplants.

Listen as Rakesh Goyal, MD, shares how the Children’s Mercy BMT program is expanding the use of transplants to successfully treat immunodeficiency, metabolic, sickle cell disease and other rare diseases.