The Bespoke Gene Therapy Consortium, a public-private partnership backed by the Foundation for the National Institutes of Health, in February published its first playbook. The playbook provides a roadmap for streamlining product development and navigation of the regulatory pathway for AAV gene therapies with the goal of getting new treatments to patients sooner. We spoke to Courtney Silverthorn, vice president of strategic alliances and innovation for the Foundation for the National Institutes of Health; and Sharon King, manager of advocacy and community engagement for Aldevron and founder and president of Taylor’s Tale; about the Bespoke Gene Therapy Consortium, its new playbook, and how it will help gene therapy developers get their medicines to patients faster.
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Accelerating Gene Editing Therapies for Rare, Neurological Conditions
Inhibiting Electrical Activity in Rare, Seizure Disorders
Improving the Function and Usability of Clothing for People with Disabilities
Treating Cardiopulmonary Disease with Inhaled Targeted Therapies
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How One Foundation Is Laying the Groundwork to Advance Treatments for an Ultra-Rare Disease
Forging a New Path for Medicine
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