The Bespoke Gene Therapy Consortium’s New Regulatory Playbook, feat. The Foundation for the National Institutes of Health and Taylor’s Tale

In this episode of the podcast we talk with Drs. Julie Gerberding and Courtney Silverthorn from the Foundation for the National Institutes of Health (FNIH). They're bringing us updates on the Bespoke Gene Therapy Consortium's new regulatory playbook that is designed to help get certain types of genetic therapies for rare diseases approved and available to patients more quickly. We're also joined by Sharon King, the Co-Founder of Taylor's Tale a non-profit that advocates on behalf of rare disease patients. She talks about why timely development of gene therapies is so important for people like her daughter, who lived with CLN1 disease.

Learn more about the FNIH and the BGTC Regulatory Playbook here.
Learn more about Taylor's Tale and the ways there are helping rare disease patients here. 

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